Most sickle cell disease patients who received the gene-editing therapy Casgevy have been free from vaso-occlusive crises for ...

November 2024 has seen a variety of biotech deals take place to advance therapies across different stages in development.

Other news stories cover once-a-year HIV prevention shots, gene therapy to reverse heart failure, and more. A bipartisan coalition of US lawmakers has drafted legislation that would force prescription ...

A new study using gene therapy from the University of Utah reversed the impact of heart failure in pigs. Can it work on ...

Researchers found a genetic therapy that could be used to reverse heart failure. A recent study found that it worked on large ...

Researchers at the meeting reported on long-term activity of commercialized gene therapies and preliminary data on ...

Heart failure has historically been irreversible, but a new study suggests that could change. At the University of Utah, ...

Avidity Biosciences' AOC platform shows promising results for genetic diseases, making it a strong buy with potential upside ...

Researchers suggest an application to FDA may be made within the next 12 months, requesting approval to carry out a human clinical trial with the gene therapy.

A new gene therapy can reverse the effects of heart failure and restore heart function in a large animal model. The therapy ...

A cure for heart failure could be on the horizon after scientists inserted a gene into ailing pigs, allowing their hearts to ...

In a new study, failing hearts nearly returned to full function in laboratory pigs after they received an experimental gene ...